European Medicines Agency (EMA) | News and press releases Follow New treatment for Niemann-Pick type C disease EMA has recommended granting a marketing authorisation in the European Union (EU) for Aqneursa (levacetylleucine) for the treatment of neurological manifestations of Niemann-Pick… https://www.ema.europa.eu/en/news/new-treatment-niemann-pick-type-c-disease ema.europa.eu
