European Medicines Agency (EMA) | What's new Follow Orphan designation: allogeneic human Wharton's jelly-derived mesenchymal stem cells Treatment of Charcot-Marie-Tooth disease, 20/05/2026 Positive https://www.ema.europa.eu/en/medicines/human/orphan-designations/eu-3-26-3237 ema.europa.eu