European Medicines Agency (EMA) | What's new Follow Orphan designation: palmitoyl-conjugated tricyclo-DNA antisense oligonucleotide 5'-Palm-C6-*GGA GAT GgC AGT TTC-3 Treatment of Duchenne muscular dystrophy, 18/07/2025 Positive https://www.ema.europa.eu/en/medicines/human/orphan-designations/eu-3-25-3084 ema.europa.eu
