Science Magazine | AAAS: Science Translational Medicine Follow Intravenous gene therapy improves life span and clinical outcomes in a feline model of Sandhoff disease | Science Translational Medicine Intravenous administration of AAV gene therapy is safe and efficacious in a feline model of Sandhoff disease. https://www.science.org/doi/10.1126/scitranslmed.adx2447 science.org
