Science Magazine | AAAS: Science Translational Medicine 中文 关注 一个三维人类视网膜模型揭示了溶酶体储存障碍中感光细胞丧失的非细胞自主且非神经元机制 |科学 转化医学 酸性鞘氨醇酶缺乏导致鞘脂信号改变,并促进溶酶体贮积病 CLN3 病的表型。 A 3D human retina model reveals a non–cell-autonomous and non-neuronal mechanism of photoreceptor loss in a lysosomal storage disorder | Science Translational Medicine science.org Science Magazine | AAAS: Science Translational Medicine 中文 RSS thenote.app