European Medicines Agency (EMA) | What's new 中文 关注 孤儿药认定：同种异体人诱导多能干细胞来源的光感受器前体细胞，用于治疗非综合征性杆细胞优势型遗传性视网膜营养不良，2026 年 5 月 20 日，结果：肯定 Orphan designation: allogeneic human induced pluripotent stem cell-derived photoreceptor precursor cells Treatment of non-syndromic inherited retinal dystrophies of the rod-dominant phenotype, 20/05/2026 Positive ema.europa.eu
