European Medicines Agency (EMA) | What's new 中文 关注 孤儿药指定:腺相关病毒载体9型编码人Gigaxonin基因,治疗巨轴索神经病,2022年4月13日,已撤回。 Orphan designation: adeno-associated virus vector serotype 9 encoding human gigaxonin gene Treatment of giant axonal neuropathy, 13/04/2022 Withdrawn ema.europa.eu